Friedreich’s Ataxia News present a study from University of Bristol in the United Kingdom about a cytokines therapy that could potentially decrease the symptoms of Friedreich’s ataxia (February 2017)

Resume from the Friedreich’s Ataxia News article, Specific Cytokines Therapy Protected Neurons in Humanized Mouse Study “A cocktail of clinically approved cytokines for other diseases shows promising neuro-protective effects in a Friedreich’s ataxia (FA) humanized mouse model. The study, “Cytokine therapy-mediated neuroprotection in a Friedreich’s ataxia mouse model” was published...

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«The incredible story of little Jayden, bubble boy, the first Québec patient successfully treated using gene therapy».

Québec media have recently covered the story of Jayden, bubble boy, the first Québec patient successfully treated using gene therapy. Jayden Duquette, five months old, was a patient of Dr. Élie Haddad, a pediatric immunologist at Ste-Justine children’s hospital in Montreal. He was born with an immune system deficiency caused...

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September 25, International Ataxia Awareness Day (IAAD), is a very special occasion for everyone to raise awareness about ataxia and to raise funds for medical research.  

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Does the treatment of rare diseases have a place in tomorrow’s economy in Quebec and Canada?

  Shire, the Irish pharmaceutical company that specializes in the treatment of rare diseases, bought the American group NPS Pharmaceuticals in February 2015 for US$5.2 billion. There have been other financial deals like this recently, always involving amounts in the billions of dollars. For some pharmaceutical companies, developing treatments for...

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